Vertex said on Tuesday that its next-generation drug gained European Commission approval for treating cystic fibrosis, a rare ...

Vertex Pharmaceuticals VRTX announced that the European Commission has approved Alyftrek ...

This photo provided by Emily’s Entourage in April 2025 shows Emily Kramer-Golinkoff, who has cystic fibrosis caused by a rare genetic mutation, during a trip to Maine. Credit: AP.

Cystic fibrosis represents one of the most common inherited genetic disorders affecting people of European descent, touching the lives of approximately 30,000 individuals in the United States ...

A scientific team has unlocked a new way to treat serious lung conditions by using specially designed nanoparticles to ...

Cystic fibrosis (CF) is a progressive genetic disease that adversely affects a person's lungs, pancreas and other vital organs, says Dr. Michael Boyle, president and CEO of the Cystic Fibrosis ...

Could next-generation gene editing mean a cure for cystic fibrosis (CF)? There's been a lot of advancement on the disease in the last decade, but there are still those living with the disease who ...

But knowledge is power, especially when it comes to managing this complex genetic condition. Cystic fibrosis might sound intimidating, but tremendous advances in treatment have transformed what it ...

Cite this: Cystic Fibrosis Gene Therapy: Successes, Failures and Hopes for the Future - Medscape - Aug 01, 2009. Abstract and Introduction Clinical Studies Using Viral Vectors ...

Cystic fibrosis (CF) is a rare autosomal recessive disorder that affects numerous systems of the body. It is a complicated ...

Cystic fibrosis is a genetic disease that damages the lungs and digestive system. Patients often die in early adulthood, but Trikafta is dramatically extending life expectancy. “Every patient in ...

Cite this: Cystic Fibrosis Gene Therapy: Successes, Failures and Hopes for the Future - Medscape - Aug 01, 2009. Abstract and Introduction Clinical Studies Using Viral Vectors ...