Along with haemolysis, people with PNH can suffer life-threatening blood clots and impaired bone marrow function. The median survival after diagnosis is 10 years, although some patients can ...

Danicopan was developed to help the approximately 10% to 20% of patients with PNH who experience this extravascular haemolysis (EVH) – a breakdown of red blood cells in the spleen, bone marrow ...

He spent his days visiting local schools and talking to the media, trying to raise awareness of PNH and the need for bone marrow donors. "He didn't view it as taking away hope," his brother said.

Biosimilar SB12 demonstrated comparable efficacy and safety for paroxysmal nocturnal hemoglobinuria (PNH) to its reference drug, showing similar outcomes across diverse patient groups.

Bone marrow transplantation can be used to treat certain blood disorders such as leukemia or immunodeficiency, but can also have serious complications such as graft-versus-host disease.