A gene therapy recently approved by the FDA to treat patients with Sickle Cell Anemia is now being administered in St. Louis.

Despite the immense potential of gene therapies, drugmakers have soured on the field. So an ambitious charity is trying to ...

The focus should be on respecting the evidence, and our lived experiences, by providing all children with an appropriate language. Proposing gene therapies for deaf children risks overlooking the ...

Researchers at the University of Minnesota have completed a first-in-human clinical trial testing a CRISPR/Cas9 gene-editing technique to help the immune system fight advanced gastrointestinal (GI) ...

A new gene therapy reversed heart failure in pigs by repairing heart function through cBIN1, showing major promise for future ...

An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life ...

A boy with an ultra-rare immune disease which can carry a “death sentence” is living a normal life after taking part in a ...

As the number of cell and gene therapies expands, it's increasingly important for long-term patient data, explained Fran ...