Sickle cell is now the fastest growing genetic condition in the United Kingdom and can cause organ damage and strokes.

Genetic disease is believed to be linked to 41 percent of U.S. infants' deaths, while more than 2 million children have a ...

Vertex Pharmaceuticals said on Tuesday its next-generation cystic fibrosis treatment has won European Union approval for a ...

Cystic fibrosis (CF) is a rare autosomal recessive disorder that affects numerous systems of the body. It is a complicated ...

A scientific team has unlocked a new way to treat serious lung conditions by using specially designed nanoparticles to ...

Cystic fibrosis is an autosomal recessive genetic disease, meaning both parents must be carriers of one of the hundreds of genetic mutations. If two people have mutations, their fetus has a 1 in 4 ...

Jonas Renner et al, Synthesis of Ionizable Lipids for Gene Delivery to the Lung Using an Ugi Four Component Reaction, Journal of the American Chemical Society (2025). DOI: 10.1021/jacs.5c04123 ...

At 7 years old, Morgan Barrett was diagnosed with cystic fibrosis. Prior to her diagnosis, she struggled to gain weight ...

A new set of standardized screening recommendations from the Cystic Fibrosis Foundation aims to reduce missed or delayed diagnosis of the genetic disorder among infants. All 50 U.S. states screen ...

Cystic fibrosis transmembrane conductance regulator (CFTR), a Cl−-ion channel, assembles into dynamic macromolecular complexes. Understanding how these complexes regulate the intracellular ...