Pat is the founding president and CEO of Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States solely focused on Duchenne muscular dystrophy (Duchenne).

vice president of Research for Parent Project Muscular Dystrophy (PPMD). "This approach could potentially add an important angle in our fight against this disease and we are pleased to see the ...

Multidisciplinary coordination across prescribing teams, nursing, laboratory medicine, finance, and infusion centers is ...

Parent Project Muscular Dystrophy, which was crucial in understanding how to manage their son’s condition and advocate for his needs. Key was the Medicaid waiver program, which allowed them to ...

The nonprofit patient advocacy group Parent Project Muscular Dystrophy (PPMD) reported that the patient received the gene therapy in early 2023, as per a report from Pfizer. "We do not yet have ...

The news was reported earlier by Stat, based on a letter posted on the website of the group Parent Project Muscular Dystrophy.

Two dose levels of a single-administration gene therapy were well-tolerated and led to functional improvements in ambulatory boys with Duchenne muscular dystrophy, interim data show.“Several microdyst ...

Columnist Patrick Moeschen highlights some key federal programs and pieces of legislation in the history of muscular dystrophy.

New Delhi: Over 200 parents from 26 states across India protested at Jantar Mantar on Wednesday with their children affected by Duchenne Muscular Dystrophy (DMD) and Muscular Dystrophy (MD ...

Colton Belluzzo was diagnosed with a form of muscular dystrophy when he was a baby ... But Colton Belluzzo's parents, Morgan and Dan, knew they didn't have many other options.