It was found that those with severe hemophilia B have less than 1% of normal factor IX activity, often experiencing spontaneous bleeding that can cause joint damage or life-threatening events.

Hemophilia disease is a rare inherited bleeding disorder. People with this genetic condition do not produce sufficient clotting factors, which can cause uncontrolled external or internal bleeding.

The results of gene therapy for hemophilia B contrast with those of factor replacement therapies, where lifelong infusions ...

Hemophilia A is a condition that keeps your blood from clotting the way it should. That means your body has problems stopping bleeding, both outside and inside your body. Your condition can be ...

When we think of hemophilia, the image that often comes to mind is that of extensive bleeding from an injury; or spontaneous bleeding in the body for no clear reason. However, for those living ...

Subsequent studies by other investigators confirmed those early results, ultimately leading to the FDA approval of ...

Blood clotting represents one of the body’s most elegant and complex protective mechanisms. This intricate process involves numerous proteins working in precise sequence – often described as a ...

Doctors warn that these could be the first signs of hemophilia, a rare inherited bleeding disorder. According to the World Federation of Hemophilia, India had the highest number of cases in 2023.

In a 13-year follow-up by St. Jude Children’s Research Hospital and University College London published in The New England ...

Managed Healthcare Executive gives C-suite executives in health plans and provider organizations news and strategies for ...

Learn how clotting factor therapy, gene therapy, and non-factor treatments are improving hemophilia prognosis and life expectancy.

A gene transfer approach to treating the bleeding disorder hemophilia B remains safe and effective long-term, as scientists ...