An experimental gene therapy seems to slow the progression of Huntington’s disease by about 75 per cent, and researchers are ...

They manage to slow down the progression of Huntington's disease using a gene therapy treatment called AMT 130.

Gene therapy is becoming a powerful way to treat challenging diseases that don’t respond to traditional treatments, and researchers now report the first success in modifying genes to slow Huntington’s ...

UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...

Scientists engineered stem cells with “interrupted” CAG repeats to break up the toxic stretch. This may stop expansion, and could improve problems in cells that model Huntington’s disease. This study ...

Huntington’s disease is a neurological (brain) condition that causes involuntary movement, changes to emotions, behavior, and thinking. Huntington’s is a genetic disease that worsens over time.

Treatment with pridopidine slowed clinical progression and maintained function, cognition, and motor performance in pre-defined analyses of a subgroup of early-stage Huntington’s disease (HD) patients ...

A Huntington’s gene therapy by UniQure has made waves after slowing disease progression by 75% in a mid-stage trial. During the Phase I/II study (NCT05243017), patients treated with a high dose of AMT ...

While Huntington’s disease is progressive and worsens over time, understanding what is to come can help someone with this condition plan for the road ahead. Huntington’s disease is a neurodegenerative ...